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Pediatrics

22-CHP-2790658-CQD–Hanna—Hunter-syndrome

Lysosomal Storage Diseases in Children: Considerations for Care

Physicians shares insights about screening, supportive care and potential therapies in development

21-RHE-2528446-Monitoring-patients-ANCA-associated-vasculitis-CQD_650x450

Studies Evaluate Rituximab to Treat Granulomatosis With Polyangiitis and Microscopic Polyangiitis in Pediatric Patients

Findings from a clinical trial and secondary analysis demonstrate clinical utility, safety

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May 10, 2022/Pediatrics/Cardiology

Study Reveals Burden of Pediatric Heart Failure in the United States

Authors find the higher death rates in children compared with adults with heart failure 'disturbing'

22-CHP-2652658 CQD- Ogonek – Rehab Tricycle Grant 650×450
April 26, 2022/Pediatrics/Rehabilitation

Adaptive Tricycles Can Help Patients Regain and Improve Function

Program donates adaptive tricycles to children with chronic conditions and serious injuries

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20-HVI-1880566-Karamlou-CQD
April 15, 2022/Pediatrics

What Would It Take To Regionalize Congenital Heart Surgery?

The evidence, the obstacles, and the opportunity to improve care

Ganaxolone Effective for Rare Form of Childhood Epilepsy (1)
April 11, 2022/Neurosciences/Epilepsy

Ganaxolone Effective for Rare Form of Childhood Epilepsy

The neuroactive steroid significantly reduces seizures related to CDKL5 deficiency disorder

22-NEU-2832861-epilepsy-evaluation-in-infant-650×450
April 6, 2022/Genomic Medicine

Prediction Model Aids in the Early Diagnosis of Dravet Syndrome

Integrates genetic and clinical data to distinguish from GEFS+ and milder epilepsies

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Deciphering Leg Pain in Children: What’s Normal and What’s Not?

Two cases highlight the importance of differentiating lower extremity pain

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